Recent Advances in Management of Rare Disease

Share this:
Published: 27 Jul 2018

This Genetic Technology TOE depicts new life sciences trends across rare disease management through gene therapy approaches. The corresponding clinical trials scenario for lysosomal storage diseases is also depicted. The Genetic Technology TechVision Opportunity Engine (TOE) presents the latest R&D developments and advances with an emphasis on opportunities to profit in the explosive field of genetic technology through technology transfer, joint ventures, and acquisitions. The complete gamut of genetic technology applications is covered including the latest developments in omics technologies; genetic, cellular, and alternative therapies; sequencing technologies; and genetically altered animals and plants. The Health & Wellness cluster tracks developments in a myriad of areas including genetic engineering, regenerative medicine, drug discovery and development, nanomedicine, nutrition, cosmetic procedures, pain and disease management and therapies, drug delivery, personalized medicine, and smart healthcare. Keywords: Ex Vivo gene therapy, lysosomal storage disease, rare diseases, genetic disorders, lentiviral therapy, Fabry's disease, Sanfilippo's syndrome, Niemann-Pick disease

Tools

Features of this research

SUBSCRIPTIONS

Help Desk

Full list of offices


For more information and general enquiries, contact Frost & Sullivan near you.

North America
tel: +1.877.463.7678

Select a location near you..